This study is NOT currently recruiting participants.
National Institute of Allergy and Infectious Diseases (NIAID)
Type: Completed Study; data analyses ongoing Gender: Male & Female Min Age: 2 Years Max Age: N/A
Referral Letter Required
Leaky SCID; Gamma Chain; Transplant; Gene Therapy; JAK 3; Natural History
Severe Combined Immune Deficiency (SCID)
National Institute of Allergy and Infectious Diseases
This protocol is a prospective natural history study in which investigators at 43 centers caring for patients with SCID Disorder in North America will participate. Investigators will: 1) evaluate and treat patients with SCID Spectrum Disorder according to their institutional practice and protocols, and also 2) enroll the same patients as subjects in this prospective natural history protocol. Thus, subjects will receive comparable baseline and follow up evaluations across all transplant centers, irrespective of the transplant (or other treatment) strategy and methods used at an individual site.
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INCLUSION CRITERIA: Subjects must be over the age of 2 and actively enrolled and receiving treatment under a SCID protocol at NIAID.
Subjects must be over the age of 2 and actively enrolled and receiving treatment under a SCID protocol at NIAID.
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